Pompe disease is induced by an accumulation of glycogen in the lysosome due to the lysosomal acid alpha-glucosidase enzyme deficiency. It is an autosomal recessive metabolic disorder that damages muscle and nerve cells throughout the body. It is a genetic disorder. Three major types of Pompe disease named classic infantile, non-classic infantile, and late-onset appear at different life stages.
MARKET DYNAMICS
The Pompe Disease market is growing due to the rise in gene therapy and enzyme replacement therapies are contributing in the growth of market. However, the lack of awareness and expensive therapy treatment is expected to hamper the growth of the global Pompe Disease market.
MARKET SCOPE
The "Pompe Disease Market Analysis to 2028" is a specialized and in-depth study of the healthcare industry with a special focus on the global market trend analysis. The report aims to provide an overview of Pompe Disease market with detailed market segmentation therapy type, molecule type, route of administration, dosage forms and geography. The Pompe Disease market is expected to witness high growth during the forecast period. The report provides key statistics on the market status of the leading players in Pompe Disease market and offers key trends and opportunities in the market.
MARKET SEGMENTATION
The Pompe Disease market is segmented on the basis of therapy type, molecule type, route of administration and dosage forms. Based on therapy type, the market is segmented as Enzyme Replacement Therapy and Substrate Reduction Therapy. On the basis of molecule type, the market segmented into Biologics and Small Molecules. On the basis of Route of Administration the market is segmented into Oral and Parenteral. On the basis of dosage form the market is segmented into Solid and Liquid
REGIONAL FRAMEWORK
The report provides a detailed overview of the industry including both qualitative and quantitative information. It provides overview and forecast of the Pompe Disease market based on various segments. It also provides market size and forecast estimates from year 2020 to 2028 with respect to five major regions, namely; North America, Europe, Asia-Pacific (APAC), Middle East and Africa (MEA) and South & Central America. The Pompe Disease market by each region is later sub-segmented by respective countries and segments. The report covers analysis and forecast of 18 countries globally along with current trend and opportunities prevailing in the region.
The report analyzes factors affecting Pompe Disease market from both demand and supply side and further evaluates market dynamics affecting the market during forecast period i.e., drivers, restraints, opportunities, and future trend. The report also provides exhaustive PEST analysis for all five regions namely; North America, Europe, APAC, MEA and South & Central America after evaluating political, economic, social and technological factors effecting the Pompe Disease market in these regions.
MARKET PLAYERS
The report covers key developments in the Pompe Disease market as organic and inorganic growth strategies. Various companies are focusing on organic growth strategies such as product launches, product approvals and others such as patents and events. Inorganic growth strategies witnessed in the market were acquisitions, and partnership & collaborations. These activities have paved way for expansion of business and customer base of market players. The market players from Pompe Disease market are anticipated to have lucrative growth opportunities in the future with the rising demand for Pompe Disease in the global market. Below mentioned is the list of few companies engaged in the Pompe Disease market.
The report also includes the profiles of key players in Pompe Disease market along with their SWOT analysis and market strategies. In addition, the report focuses on leading industry players with information such as company profiles, components and services offered, financial information of last 3 years, key development in past five years.
- Amicus Therapeutics
- BioMarin Pharmaceutical
- Genzyme
- Audentes Therapeutics
- EpiVax
- Oxyrane
- Sangamo BioSciences
- Valerion Therapeutics
- Centogene
- Sanofi
The Insight Partner's dedicated research and analysis team consists of experienced professionals with advanced statistical expertise and offers various customization options in the existing study.